Last Update: May 05, 2026
A Single Arm, Multicenter, Open-label Extension (OLE) Trial to Evaluate Long-term Safety and Tolerability of Pelacarsen (TQJ230) in Participants Who Completed the Parent Lp(a)HORIZON Trial
ClinicalTrials.gov Identifier:
Novartis Reference Number:CTQJ230A12301E1
All compounds are either investigational or being studied for (a) new use(s). Efficacy and safety have not been established. There is no guarantee that they will become commercially available for the use(s) under investigation.

Study Description

This open-label extension study will provide post-trial access to pelacarsen (TQJ230) to participants who have successfully completed the double-blind parent study (CTQJ230A12301). This study will evaluate long-term safety and tolerability of pelacarsen (TQJ230) 80 mg Once a month (QM) in participants with established cardiovascular disease and elevated Lp(a) who completed the parent study (CTQJ230A12301).

Cardiovascular Disease and Lipoprotein(a)
Phase3
Recruiting
5700
May 11, 2026
Jan 09, 2030
All
18 Years - 100 Years (Adult, Older Adult)

Interventions

Drug

Pelacarsen (TQJ230)

pelacarsen 80mg s.c. monthly

Eligibility Criteria

Inclusion Criteria:

* Participants who have provided informed consent prior to initiation of any study-specific activities/procedures.
* Participants who have completed the parent study EOS visit while still on assigned investigational product.

Exclusion Criteria:

* Participants who for any reason permanently discontinued or have interrupted the investigational product for continuous 6 months at EOS during the parent study.
* Participants who have a history or evidence of any clinically significant disorder, condition, or disease that in the opinion of the investigator or Novartis physician (if consulted), would put the participant at risk or interfere with the study participation, including, but not restricted to conditions outlined in Table 6-3 and Table 6-5.
* Participants are receiving another investigational drug or device before the open-label treatment period.
* Participants have a known sensitivity to the study drug and are deemed as unsuited for the study by the Investigator at Screening visit.

Other protocol-defined inclusion/exclusion criteria may apply.

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Mar del Plata,Buenos Aires,7600,Argentina

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CABA,Buenos Aires,1407,Argentina

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Caba,Buenos Aires,C1119acn,Argentina

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Ramos Mejía,Buenos Aires,B1704etd,Argentina

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CABA,Buenos Aires F.D.,1426,Argentina

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Córdoba,Córdoba Province,5000,Argentina

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San Miguel de Tucumán,San Miguel de Tucuman,4000,Argentina

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San Miguel de Tucumán,San Miguel de Tucuman,T4000icl,Argentina

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Rosario,Santa Fe Province,2000,Argentina

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Rosario,Santa Fe Province,S200cvd,Argentina

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Santa Fe,Santa Fe Province,S3000fwo,Argentina

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Buenos Aires,C1280aeb,Argentina

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Caba,C1426,Argentina

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Capital Federal,C1023aab,Argentina

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Corrientes,W3400cds,Argentina

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San Luis,D5702jrs,Argentina

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Camperdown,New South Wales,2050,Australia

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Liverpool,New South Wales,2170,Australia

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Chemside,Queensland,4032,Australia

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Woolloongabba,Queensland,4102,Australia

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Clayton,Victoria,3168,Australia

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Perth,Western Australia,6000,Australia

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Linz,4021,Austria

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Salzburg,5020,Austria

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Vienna,1210,Austria

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Huy,4500,Belgium

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Brussels,Brussels Capital,1070,Belgium

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Genk,Limburg,3600,Belgium

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Aalst,Oost Vlaanderen,9300,Belgium

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Bruges,8000,Belgium

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Dendermonde,9200,Belgium

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Santo André,São Paulo,09090-790,Brazil

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São Paulo,São Paulo,01323 000,Brazil

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Vitória,Espírito Santo,29055-450,Brazil

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Goiânia,Goiás,74605-020,Brazil

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Belo Horizonte,Minas Gerais,30150-270,Brazil

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Belo Horizonte,Minas Gerais,30150-320,Brazil

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Juiz de Fora,Minas Gerais,36033-318,Brazil

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Uberlândia,Minas Gerais,38400 500,Brazil

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Curitiba,Paraná,80730-150,Brazil

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Canoas,Rio Grande do Sul,92425 900,Brazil

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Porto Alegre,Rio Grande do Sul,90880-480,Brazil

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Aracaju,Sergipe,49055-530,Brazil

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Campinas,São Paulo,13060 080,Brazil

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Campinas,São Paulo,13092133,Brazil

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Ribeirão Preto,São Paulo,14026-020,Brazil

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Santo André,São Paulo,09060-870,Brazil

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Sao Jose Rio Preto,São Paulo,15015-750,Brazil

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Sao Jose Rio Preto,São Paulo,15090 000,Brazil

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São Paulo,São Paulo,04005-003,Brazil

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São Paulo,São Paulo,04266 010,Brazil

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Rio de Janeiro,20241-180,Brazil

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Burgas,8001,Bulgaria

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Pernik,2300,Bulgaria

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Pleven,5800,Bulgaria

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Plovdiv,4000,Bulgaria

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Rousse,7002,Bulgaria

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Sofia,1233,Bulgaria

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Beijing,Beijing Municipality,100013,China

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Lanzhou,Gansu,730030,China

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Foshan,Guangdong,528000,China

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Guangzhou,Guangdong,510030,China

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Guangzhou,Guangdong,510080,China

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Harbin,Heilongjiang,150000,China

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Changsha,Hunan,410003,China

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Changsha,Hunan,410008,China

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Changsha,Hunan,410011,China

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Nanjing,Jiangsu,210009,China

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Nanjing,Jiangsu,210029,China

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Nanjing,Jiangsu,211166,China

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Suzhou,Jiangsu,215004,China

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Xuzhou,Jiangsu,221003,China

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Changchun,Jilin,130021,China

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Dalian,Liaoning,116011,China

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Shenyang,Liaoning,110004,China

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Shenyang,Liaoning,110016,China

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Jinan,Shandong,250013,China

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Xian,Shanxi,710061,China

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Chengdu,Sichuan,610041,China

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Ürümqi,Xinjiang,830054,China

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Hangzhou,Zhejiang,310014,China

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Hangzhou,Zhejiang,310016,China

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Wenzhou,Zhejiang,325000,China

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Beijing,100191,China

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Xiamen,361004,China

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San Gil,684031,Colombia

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Cali,Valle del Cauca Department,760032,Colombia

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Bogotá,111211,Colombia

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Medellín,050037,Colombia

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Kroměříž,Czech Republic,767 55,Czechia

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Brno,602 00,Czechia

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Brno,625 00,Czechia

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Broumov,550 01,Czechia

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Kolín,280 20,Czechia

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Most,434 01,Czechia

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Ostrava,Zabreh,700 30,Czechia

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Pardubice,532 03,Czechia

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Prague,128 08,Czechia

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Trutnov,460 63,Czechia

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Uherské Hradiště,686 01,Czechia

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Valašské Meziříčí,75742,Czechia

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Chlumec nad Cidlinou,Chlumec Nad Cidlinou,503 51,Czechia

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Louny,Czech Republic,440 01,Czechia

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Ústí nad Labem,Czech Republic,400 01,Czechia

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Brandýs nad Labem,250 01,Czechia

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Prague,110 00,Czechia

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Hlučín,748 01,Czechia

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Hodonín,695 01,Czechia

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Jihlava,586 01,Czechia

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Liberec,460 01,Czechia

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Liberec,460 05,Czechia

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Gelnhausen,63571,Germany

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Ulm,89077,Germany

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Larissa,411 10,Greece

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Debrecen,Hajdu Bihar Megye,4032,Hungary

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Dehradun,Uttarakhand,248001,India

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Guntur,Andhra Pradesh,522001,India

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Ahmedabad,Gujarat,380054,India

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Ahmedabad,Gujarat,380060,India

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Vadodara,Gujarat,390022,India

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Belagavi,Karnataka,590010,India

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Mangalore,Karnataka,575018,India

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Manipal,Karnataka,576104,India

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Mysore,Karnataka,570015,India

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Kochi,Kerala,682018,India

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Kochi,Kerala,682027,India

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Kochi,Kerala,682041,India

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Nagpur,Maharashtra,440008,India

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Nagpur,Maharashtra,440012,India

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Nagpur,Maharashtra,440025,India

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Nashik,Maharashtra,422005,India

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Pune,Maharashtra,411004,India

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Pune,Maharashtra,411028,India

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Pune,Maharashtra,411045,India

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New Delhi,National Capital Territory of Delhi,110075,India

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Coimbatore,Tamil Nadu,641037,India

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Hyderabad,Telangana,500034,India

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Hyderabad,Telangana,500082,India

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Secunderabad,Telangana,500003,India

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Ghaziabad,Uttar Pradesh,201012,India

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Lucknow,Uttar Pradesh,226003,India

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New Delhi,110025,India

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Haifa,3436212,Israel

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Beersheba,8457108,Israel

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Haifa,3104802,Israel

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Jerusalem,9112001,Israel

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Petah Tikva,4941492,Israel

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Ramat Gan,5265601,Israel

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Bergamo,BG,24127,Italy

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Milan,MI,20138,Italy

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Milan,MI,20149,Italy

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Milan,MI,20162,Italy

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Rozzano,MI,20089,Italy

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Ancona,AN,60128,Italy

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Florence,FI,50134,Italy

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Pozzilli,IS,86077,Italy

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Milan,MI,20132,Italy

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Palermo,PA,90127,Italy

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Perugia,PG,06129,Italy

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Pisa,PI,56124,Italy

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Pisa,PI,56126,Italy

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Roma,RM,00161,Italy

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Roma,RM,00189,Italy

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Varese,VA,21100,Italy

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Naples,80131,Italy

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Seto,Aichi-ken,4898642,Japan

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Kitakyushu,Fukuoka,8028555,Japan

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Kure,Hiroshima,737-0023,Japan

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Kawasaki,Kanagawa,2120021,Japan

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Miyhazaki,Miyazaki,8802102,Japan

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Chuo-ku,Tokyo,1030027,Japan

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Itabashi-ku,Tokyo,1738610,Japan

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Tiel,Gelderland,4002 wp,Netherlands

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Sneek,Provincie Friesland,8601 zk,Netherlands

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Apeldoorn,Gelderland,7334 dz,Netherlands

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Arnhem,Gelderland,6815 ad,Netherlands

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Heerlen,Limburg,6419 pc,Netherlands

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Tilburg,North Brabant,5042 ad,Netherlands

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Amsterdam,North Holland,1090 hm,Netherlands

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Heemstede,North Holland,2035 rc,Netherlands

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Leiderdorp,South Holland,2353 ga,Netherlands

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Amersfoort,3813 tz,Netherlands

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Hardenberg,7770 se,Netherlands

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Utrecht,3584 cx,Netherlands

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Venlo,5912 bl,Netherlands

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Bielsko-Biala,43-316,Poland

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Gdansk,80-214,Poland

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Gdynia,81-157,Poland

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Lodz,93-338,Poland

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Tarnów,33-100,Poland

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Coimbra,3004-561,Portugal

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Guimarães,4835-044,Portugal

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Setúbal,2910-549,Portugal

Research and Cardiovascular Corp

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